About Us
Our story, our mission, and why we exist.
Our story, our mission, and why we exist.
Our Mission
To accelerate the development of treatments and a cure for Autosomal Dominant Leukodystrophy by connecting patients, researchers, and industry, and funding the science that moves the needle.
The ADLD Center is a nonprofit organization dedicated to one goal: ending Autosomal Dominant Leukodystrophy. We operate at the intersection of patient advocacy, clinical research, and industry partnership, accelerating every part of the pipeline that leads to a cure.
Funding Research
Grants at Mayo Clinic, Henry Ford Health, and the Orphan Disease Center at UPenn, up to $50,000 per grant per year.
Running Clinical Trials
We initiated the first-in-human ADLD n=1 clinical trial and are paving the way for multi-patient trials by 2026.
Natural History Study
A global, remote study tracking ADLD progression to power synthetic control arms in future FDA trials.
Patient Support
Education, community meetups, and resources that help patients and families navigate their ADLD journey.